Stem Cell for Duchenne Muscular Dystrophy. Duchenne muscular dystrophy (DMD) is the most common and serious form of
muscular dystrophy. One out of every 3500 boys is born with the
disorder, and it is invariably fatal. Until recently, there was little
hope that the widespread muscle degeneration that accompanies this
disease could be combated.
However, stem cell therapy now offers that hope.
Like other
degenerative disorders, DMD is the result of loss of cells that are
needed for correct functioning of the body. In the case of DMD, a vital
muscle protein is mutated, and its absence leads to progressive
degeneration of essentially all the muscles in the body.
To begin to approach a therapy for this condition, we must provide a new
supply of stem cells that carry the missing protein that is lacking in
DMD.
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